Pontocerebellar Hypoplasia Type 3 With Two Novel PCLO Gene Mutations: A Case Report

Pontocerebellar hypoplasia Type III (PCH3) is a rare, autosomal recessive neurodegenerative disorder linked to mutations in the PCLO gene, previously reported only in Omani populations. It presents with progressive microcephaly, intractable epilepsy, optic atrophy, and severe developmental delay. He...

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Autori principali: Sethapong Lertsakulbunlue, Panithi Piyachon, Pitchaya Pichantianchai, Thanapat Chivaruangrot, Piradee Suwanpakdee, Boonchai Boonyawat
Natura: Articolo
Lingua:inglese
Pubblicazione: Wiley 2025-01-01
Serie:Case Reports in Pediatrics
Accesso online:http://dx.doi.org/10.1155/crpe/1955363
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