Therapeutic potential of allogeneic iPS cell-derived RPE transplantation for RPE65-LCA
Purpose: To evaluate the safety and therapeutic effects of induced pluripotent stem (iPS) cell-derived retinal pigment epithelium (RPE) transplantation for RPE65-associated Leber congenital amaurosis (RPE65-LCA). Observations: A 46-year-old male patient with RPE65-LCA underwent allogeneic iPS cell-d...
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Main Authors: | Akiko Maeda, Daiki Sakai, Satoshi Yokota, Midori Yamamoto, Sunao Sugita, Yasuhiko Hirami, Michiko Mandai, Tadao Maeda, Masayo Takahashi, Yasuo Kurimoto |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2025-09-01
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Series: | American Journal of Ophthalmology Case Reports |
Subjects: | |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2451993625001367 |
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