Niemann-Pick Disease: Seven Questions about it

Acid sphingomyelinase deficiency is a rare hereditary disease caused by enzyme deficiency due to mutations in the SMPD1 gene. Decreased enzyme activity leads to accumulation of sphingomyelin in lysosomes. This disease is characterized by wide diversity of clinical manifestations: from infantile neur...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Autori principali: Nato D. Vashakmadze, Nataliya V. Zhurkova
Natura: Articolo
Lingua:inglese
Pubblicazione: "Paediatrician" Publishers LLC 2023-12-01
Serie:Вопросы современной педиатрии
Soggetti:
Accesso online:https://vsp.spr-journal.ru/jour/article/view/3357
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne!!