Generation and differentiation of an induced pluripotent stem cell line (FMCPGHi006-A) from a patient with Duchenne muscular dystrophy carrying exons 42–43 deletion in the DMD gene
Duchenne muscular dystrophy (DMD) is an X-linked recessive genetic disorder characterized by severe progressive muscle atrophy. Although treatments for respiratory complications have improved, dilated cardiomyopathy (DCM) with heart failure remains the leading cause of death in patients with DMD. We...
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Main Authors: | Yue Chang, Xiuyi Ai, Ruo Wu, Shu Zhang, Pei Zhang, Shiwen Wu |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2025-09-01
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Series: | Stem Cell Research |
Online Access: | http://www.sciencedirect.com/science/article/pii/S1873506125001060 |
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