Alipogene tiparvovec: a long journey of risk-benefit ratio assessment of gene therapy products

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Alipogene tiparvovec: a long journey of risk-benefit ratio assessment of gene therapy products

According to EMA, advanced therapy medicinal products include, inter alia, therapeutic systems containing nucleic acids used for replacement or repair of genetic defects. Alipogen tiparvovec, a medicine containing genetic material for treatment of hereditary deficiency of lipoprotein lipase, meets t...

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Bibliographic Details
Main Authors:	R. N. Alyautdin, B. K. Romanov, A. P. Pereverzev, A. O. Chikalo, N. D. Bunyatyan, V. A. Merkulov, A. N. Mironov
Format:	Article
Language:	Russian
Published:	Federal State Budgetary Institution ‘Scientific Centre for Expert Evaluation of Medicinal Products’ of the Ministry of Health of the Russian Federation (FSBI ‘SCEEMP’) 2018-02-01
Series:	Регуляторные исследования и экспертиза лекарственных средств
Subjects:	алипоген типарвовек наследственный дефицит липопротеинлипазы средства передовой терапии alipogene tiparvovec hereditary lpl deficiency advanced therapy medicinal products
Online Access:	https://www.vedomostincesmp.ru/jour/article/view/24
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